Dr Sandip Patel Previews the Highly Anticipated 50th Anniversary of WCLC
The 2024 World Conference on Lung Cancer (WCLC) marks the 50th anniversary of the International Association for the Study of Lung Cancer. Sandip Patel, MD, joined for an interview looking forward to the unique features of this year's meeting.
Pegcetacoplan May Reduce Fatigue in PNH Accompanied by Anemia
Findings from a post hoc analysis of 3 clinical trials support the switching to or initiation of pegcetacoplan to manage fatigue for patients with paroxysmal nocturnal hemoglobinuria (PNH) that is accompanied by mild to moderate anemia.
Nusinersen May Improve Fatiguability in SMA, but More Research Is Needed
Findings from an Italian cohort suggest that nusinersen may benefit fatigue measures in patients with spinal muscular atrophy (SMA) type III; however, drawing definitive conclusions in this area remains difficult.
From Persistent to Preventable: The Impact of Policy on the Future of Forever Chemicals
This second installment on the threat of forever chemicals examines the impactful policies brought about during the Biden-Harris administration that are set to play a role in the future manufacturing, use, and monitoring of these harmful substances.
SMN Depletion May Increase Risk of Liver Damage, Fatty Liver in SMA
A retrospective, single-center cohort study utilized liver ultrasound, serum collection, and proteome analysis to draw associations between spinal motor neuron (SMN) protein depletion and heightened risk for fatty liver disease in spinal muscular atrophy (SMA).
Real-World Outcomes Not Always Reflected in Clinical Trials: Dr Maria Amaya
Maria Amaya, MD, PhD, University of Colorado School of Medicine, explores discrepancies between real-world data and clinical trial outcomes, as well as her experience ensuring the reliability of real-world analysis.
Never Give Up on Your Diagnosis: Caitlin Kindberg's Message to Patients With Idiopathic Hypersomnia
Caitlin Kindberg, a patient advocate from Nashville, Tennessee, discusses her experience finding proper treatment for idiopathic hypersomnia and the challenges associated with living with this condition.
The Benefits of More Sickle Cell Retinopathy Screening for Patients With SCD
A systematic analysis that reviewed screening for sickle cell retinopathy in patients with sickle cell disease (SCD) underscores the importance of advanced imaging measures and further research on screening implementation methods.