Navigating Hope, Risk, and the Unknown in a Changing DMD Treatment Landscape
DMD Gene Therapy Shows Efficacy, Safety in Patients Treated at 2 Years Old
Delandistrogene Moxeparvovec Shows Long-Term Safety, Tolerability in Pooled Trial Data
Quantitative Magnetic Resonance Outcomes Suggest Gene Therapy Slows DMD Progression
Studies Highlight Heavy Burden on Caregivers of Patients With DMD