Gene Therapy

Latest News

gene therapy | Image Credit: © RFBSIP - stock.adobe.com
Expanding Broader Patient Access to CGTs

April 30th 2025

Key trends and challenges are shaping the next era of advanced therapies, from FDA momentum to broader patient access.

At 6 months, 81% of wounds showed 50% or more healing vs 16% of 43 matched control wounds treated with standard of care in the VIITAL study. | Image credit: wladimir1804 - stock.adobe.com
FDA Approves Prademagene Zamikeracel for Recessive Dystrophic Epidermolysis Bullosa

April 29th 2025

The consensus guidelines aim to provide practical guidance for institutions administering gene therapy in a commercial or trial setting. | Image credit: CrazyJuke - stock.adobe.com
Consensus Guidelines Aim to Optimize DMD Gene Therapy Delivery

April 18th 2025

Real-world data suggest delandistrogene moxeparvovec is well-tolerated and effective in patients with DMD. | Image credit: natali_mis - stock.adobe.com
Real-World Study Suggests DMD Gene Therapy Is Safe, Effective

March 26th 2025

Delandistrogene moxeparvovec is an adeno-associated virus vector-based gene therapy approved for the treatment of DMD. Image credit: natali_mis - stock.adobe.com
Delandistrogene Moxeparvovec Shows Long-Term Impacts at 3 and 5 Years in DMD

March 21st 2025

More News

AJMC Managed Markets Network Logo
CH LogoCenter for Biosimilars Logo