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Hemophilia

Latest News

Concept of FDA approved | Image credit: wladimir1804-stock.adobe.com
FDA Approves One-Time Gene Therapy Fidanacogene Elaparvovec for Hemophilia B

April 26th 2024

The FDA has approved fidanacogene elaparvovec-dzkt (Beqvez; Pfizer), a gene therapy administered in a one-time dose, for certain patients with moderate to severe hemophilia B.

HemophiliaA | Image Credit: MQ-Illustrations - stock.adobe.com
Males With Hemophilia A Report Physical, Mental Burdens of Disease Regardless of Severity

April 25th 2024

Hemophilia defined | Image Credit: VitezslavVylicil - stock.adobe.com
Long-Term Data Demonstrate Emicizumab Safety, Efficacy in Hemophilia A

April 16th 2024

Hemophilia | Image Credit: lexiconimages - stock.adobe.com
Study Suggests Walking 10K Steps Daily Improves QOL in Severe Hemophilia

April 12th 2024

Blood Cells | Image Credit: © Катерина Євтехова - stock.adobe.com
Clot Formation, Fibrinolysis Assays May Help Show Important Differences Between Hemophilia A Treatments

April 6th 2024

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