Hemophilia

Gene Therapy for Hemophilia B Shows Positive Results in Phase 3 Trial

June 25th 2021, 1:30pm

Article

The company, uniQure, said it is the largest group of patients with hemophilia B to receive a single gene therapy investigational product so far. 

Study Finds Inhibitors Develop in Nonsevere Hemophilia A Earlier Than Previously Reported

October 30th 2020, 8:09pm

Article

Up until now, it was thought most patients with hemophilia A developed inhibitors in middle-age. A new study suggests it usually happens in the early teens.

Gaps Remain Between European Regions for Hemophilia Care Despite Improvements

July 17th 2020, 10:00pm

Article

Hemophilia care principles have been on the rise in Europe over the course of the last decade, however, differing regions and policies on the continent reveal gaps in access to various treatments and specialty services.

Prevalence of Hemophilia Worldwide Is Triple That of Previous Estimates, New Study Says

September 10th 2019, 1:00am

Article

The meta-analysis showed that more than 1,125,000 men around the world have the inherited bleeding disorder; 418,000 of those have a severe version of the mostly undiagnosed disease. Previously, only 400,000 people globally were estimated to have hemophilia.