Opinion|Videos|June 26, 2024

Efficacy End Points For PNH Treatment

Dr Haumschild continues leading an expert discussion surrounding key strategies and pain points in PNH treatment.

Video content above is prompted by the following:

  • Please describe the significance of the different efficacy end points explored for paroxysmal nocturnal hemoglobinuria treatments (eg, lactate dehydrogenase levels, hemoglobin concentrations, absolute reticulocyte count (ARC) levels, transfusion avoidance, Functional Assessment of Chronic Illness Therapy–Fatigue).

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